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Argininosuccinic Aciduria MeSH Descriptor Data 2026
Rare autosomal recessive disorder of the urea cycle which leads to the accumulation of argininosuccinic acid in body fluids and severe HYPERAMMONEMIA. Clinical features of the neonatal onset of the disorder include poor feeding, vomiting, lethargy, seizures, tachypnea, coma, and death. Later onset results in milder set of clinical features including vomiting, failure to thrive, irritability, behavioral problems, or psychomotor retardation. Mutations in the ARGININOSUCCINATE LYASE gene cause the disorder.
Entry Term(s)
ASA Deficiency
ASL Deficiency
Arginino Succinase Deficiency
Argininosuccinase Deficiency
Argininosuccinate Acidemia
Argininosuccinate Lyase Deficiency
Argininosuccinic Acid Lyase Deficiency
Argininosuccinic Acidemia
Argininosuccinicaciduria
Argininosuccinyl-Coa Lyase Deficiency
Arginosuccinase Deficiency
Asauria
Inborn Error of Urea Synthesis, Arginino Succinic Type
Rare autosomal recessive disorder of the urea cycle which leads to the accumulation of argininosuccinic acid in body fluids and severe HYPERAMMONEMIA. Clinical features of the neonatal onset of the disorder include poor feeding, vomiting, lethargy, seizures, tachypnea, coma, and death. Later onset results in milder set of clinical features including vomiting, failure to thrive, irritability, behavioral problems, or psychomotor retardation. Mutations in the ARGININOSUCCINATE LYASE gene cause the disorder.